Congenital Muscular Dystrophy (CMD) Outcome measures
The 173rd ENMC/TREAT-NMD Workshop organized by Prof. Francesco Muntoni, Prof. Eugenio Mercuri, Dr. Carsten Bonnemann and Dr. Anne Rutkowski (Cure CMD) complemented current efforts to support congenital muscular dystrophy clinical trial readiness, including launch of an international CMD registry and development of CMD Care Guidelines. An opening introduction by Dr. Jeremy Hobart and Dr. Stefan Cano […]